Gene therapies to treat rheumatoid arthritis have evolved slowly, but one is ready to move into human trials and an ...

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...

Researchers have demonstrated, for the first time in the world using mice, the ability to overcome significant challenges in ...

Job cuts in Cambridge and Plainville are the second workforce reduction planned for the facilities in the past three months.

International collaborations, refined gene-editing protocols, and targeted immunologic maneuvers keep the cancer gene therapy ...

For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that ...

The cuts at two Massachusetts plants follow further site closures and layoffs across the company over the past few years.

Previous research has shown that voretigene neparvovec administered subretinally early in childhood for RPE65-mediated ...

Based on this, we have developed a new approach to enhance the efficiency of rAAV-mediated gene expression. This approach uses co-infection with a transgene-containing vector and a second vector ...

Oxford, UK - 5 February 2025: OXB (LSE: OXB), a quality and innovation-led cell and gene therapy CDMO, today announces the ...

Researchers are enhancing the best features of AAV capsids and overcoming their limitations to accelerate gene-based therapies.