Scholar Rock, a Boston-area biopharma company, announced the submission of a biologics license application and request of priority review for apitegromab to treat spinal muscular atrophy.
Jeremy Bray, who has Type 2 spinal muscular atrophy — a rare degenerative disease that has gradually robbed him of the ability to move his muscles — says he cannot wait for Canada's Drug ...
So the outcome and the long-term outlook for our patients with SMA, particularly in the adult populations are that they are now stronger and living longer. And so as a result of that, they're able ...
Copyright 2025 The Associated Press. All Rights Reserved. A spine-stimulating implant already being tested for paralysis might also aid neurodegenerative diseases ...
Background: Spinal and bulbar muscular atrophy (SBMA) or Kennedy disease [OMIM: 313200] is a rare X-linked neuromuscular disease. Patients commonly present with muscle cramps, tremors, leg weakness, ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results