Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single ...
Columnist Shalom Lim is working with Julia Cameron's popular book "The Artist's Way" as a route to develop his creative self, ...
Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single Elevidys infusion.
As a parent and caregiver to three sons with DMD, columnist Betty Vertin's definition of what success looks like has changed over the years.
The FDA has granted fast track designation to DYNE-101, a therapy for myotonic dystrophy type 1 (DM1) now in testing in a ...